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Our advanced gene therapy technology capitalizes on our differentiated knowledge of direct-to-brain administration of AAV vectors, allowing us to precisely target the causes of disease.
Extraordinary progress in developing therapies for CNS diseases with lead programs in neurodegenerative lysosomal storage disorders.
Our team is committed to developing pioneering therapies that will transform the lives of children affected by these devastating diseases.
Our team is committed to fulfilling gene therapy’s potential by developing pioneering therapies that will transform the lives of children affected by these devastating diseases.
News, press releases, and more.
Paris, France — 13 April 2021 at 06:00pm — Lysogene (FR0013233475 – LYS), a phase…
Paris, France — 25 January 2021 at 08:00am — Lysogene (FR0013233475 – LYS), a phase…
Paris, France — 15 January 2021 at 06:00pm — Lysogene (FR0013233475 – LYS), a phase…
LYS-GM101 is Lysogene’s second CNS gene therapy program to enter clinic Trial enrollment expected to…
Decrease in heparan sulfate concentration in cerebrospinal fluid Decrease in GM2 and GM3 ganglioside in…
Paris, France — 18 December 2020 at 08:00am — Lysogene (FR0013233475 – LYS), a phase…
Cash and cash equivalents of €22.1 million1 as of 30 September 2020 Paris, France —…
Paris, France — 15 October 2020 at 08:00am — Lysogene (FR0013233475 – LYS), a Phase…
Cash position of €23.8m as of 30 June 2020 strengthened by a €7.7m capital increase ledby OrbiMed and Sarepta, extending cash runway to Q4 2021
Cash and cash equivalent of €23.8 million1 as of 30 June 2020 FDA letter on…
Valuable information designed to provide knowledge and insights to patients, families, and caregivers.
Mucopolysaccharidosis type IIIA (MPS IIIA), or Sanfilippo syndrome type A, is a rare neurodegenerative lysosomal storage disorder characterized by intractable behavioral problems and developmental regression that typically appears in infancy or early childhood.
GM1 gangliosidosis, or Landing disease, is a rare inherited neurodegenerative lysosomal storage disorder characterized by severe cognitive and motor developmental delays.
Fragile X syndrome (FXS) is the most common inherited cause of autism spectrum disorder and affects approximately 1 in 4,000 to 5,000 boys and 1 in 8,000 girls.
Neuronopathic Gaucher and Parkinson’s disease are both associated with mutations in the GBA1 gene and cause neurological symptoms.
