Clinical Trials

At Lysogene, we seek to achieve the impossible by developing breakthrough gene therapies to improve the lives of central nervous system disorder patients. Our lead programs focus on neurodegenerative lysosomal disorders.

This mission is only made possible through partnerships with the courageous patients and families who share our dedication to finding cures for these devastating diseases. To find out more about whether our clinical trials are right for you and your family, contact the Patient Advocacy Team.
MPS IIIA / Sanfilippo Syndrome
GM1 Gangliosidosis
GM1 Natural History Study

Lysogene COVID-19 update

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Don’t hesitate to contact us if you need more help.